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List of works by Sofia Benkhelifa-Ziyyat

Allele-specific silencing therapy for Dynamin 2-related dominant centronuclear myopathy

scientific article published on 15 December 2017

An embryonic CaVβ1 isoform promotes muscle mass maintenance via GDF5 signaling in adult mouse

scientific article published on 01 November 2019

Antisense pre-treatment increases gene therapy efficacy in dystrophic muscles.

scientific article published on 4 July 2016

Changes in the accessibility of the HIV-1 Integrase C-terminus in the presence of cellular proteins.

scientific article

Clathrin plaques and associated actin anchor intermediate filaments in skeletal muscle

scientific article published on 02 January 2019

Cross-Presentation of Skin-Targeted Recombinant Adeno-associated Virus 2/1 Transgene Induces Potent Resident Memory CD8+ T Cell Responses

scientific article published on 19 February 2019

Dystrophin Threshold Level Necessary for Normalization of Neuronal Nitric Oxide Synthase, Inducible Nitric Oxide Synthase, and Ryanodine Receptor-Calcium Release Channel Type 1 Nitrosylation in Golden Retriever Muscular Dystrophy Dystrophinopathy.

scientific article published on 8 June 2016

Gene Therapy via Trans-Splicing for LMNA-Related Congenital Muscular Dystrophy.

scientific article published on 30 December 2017

Intradermal Immunization with rAAV1 Vector Induces Robust Memory CD8(+) T Cell Responses Independently of Transgene Expression in DCs.

scientific article

Intramuscular scAAV9-SMN injection mediates widespread gene delivery to the spinal cord and decreases disease severity in SMA mice.

scientific article

Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice

scientific article published on 30 November 2010

Phosphorylation of MafA is essential for its transcriptional and biological properties

scientific article published in July 2001

Quantification of lentiviral vector copy numbers in individual hematopoietic colony-forming cells shows vector dose-dependent effects on the frequency and level of transduction.

scientific article

RFX1 and RFX3 Transcription Factors Interact with the D Sequence of Adeno-Associated Virus Inverted Terminal Repeat and Regulate AAV Transduction

scientific article published on 9 January 2018

Transduction Efficiency of Adeno-Associated Virus Serotypes After Local Injection in Mouse and Human Skeletal Muscle

scientific article published on 24 January 2020

mafA, a novel member of the maf proto-oncogene family, displays developmental regulation and mitogenic capacity in avian neuroretina cells.

scientific article