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Gene Therapy via Trans-Splicing for LMNA-Related Congenital Muscular Dystrophy.

scientific article published on 30 December 2017

Author/s

author: Gisèle Bonne, Astrid Brull, Sofia Benkhelifa-Ziyyat, Marc Bitoun, Anne Bertrand

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Publication date
December 30, 2017
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