List of works by Hubert Gaspar

A modified γ-retrovirus vector for X-linked severe combined immunodeficiency

scientific article

Clinical and immunological features in a cohort of patients with partial DiGeorge syndrome followed at a single center

scientific article published on 23 April 2019

Consensus approach for the management of severe combined immune deficiency caused by adenosine deaminase deficiency

scientific article published on 05 September 2018

Gammaretrovirus-mediated correction of SCID-X1 is associated with skewed vector integration site distribution in vivo

scientific article published in August 2007

Gene therapy: X-SCID transgene leukaemogenicity

scientific article

Improving cellular therapy for primary immune deficiency diseases: recognition, diagnosis, and management

scientific article

Insertion sites in engrafted cells cluster within a limited repertoire of genomic areas after gammaretroviral vector gene therapy

scientific article published on 23 August 2011

Insertional mutagenesis combined with acquired somatic mutations causes leukemogenesis following gene therapy of SCID-X1 patients

scientific article published on September 2008

Lentiviral vectors containing an enhancer-less ubiquitously acting chromatin opening element (UCOE) provide highly reproducible and stable transgene expression in hematopoietic cells

scientific article published on 24 April 2007

Perforin gene transfer into hematopoietic stem cells improves immune dysregulation in murine models of perforin deficiency

scientific article published on 19 December 2014

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