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List of works by Giulia Massaro

AAV9 intracerebroventricular gene therapy improves lifespan, locomotor function and pathology in a mouse model of Niemann-Pick type C1 disease

article

Correction: Impaired cellular bioenergetics caused by GBA1 depletion sensitizes neurons to calcium overload

scientific article published on 09 March 2020

Epilepsy Gene Therapy Using an Engineered Potassium Channel

article

Fetal gene therapy for neurodegenerative disease of infants

article

Impaired cellular bioenergetics caused by GBA1 depletion sensitizes neurons to calcium overload

scientific article published on 04 November 2019

Neonatal brain-directed gene therapy rescues a mouse model of neurodegenerative CLN6 Batten disease

scientific article published on 01 December 2019

Systemic AAV9 gene therapy using the synapsin I promoter rescues a mouse model of neuronopathic Gaucher disease but with limited cross-correction potential to astrocytes

scientific article published on 10 January 2020

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