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List of works by Alex A Mireault

CRISPR-Cas9 corrects Duchenne muscular dystrophy exon 44 deletion mutations in mice and human cells

scientific article published on 06 March 2019

Enhanced CRISPR-Cas9 correction of Duchenne muscular dystrophy in mice by a self-complementary AAV delivery system

scientific article published on 19 February 2020

Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy

scientific article published in Science

Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy.

scientific article published in November 2017

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