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List of works by Thierry VandenDriessche

A Novel Platform for Immune Tolerance Induction in Hemophilia A Mice

scientific article published on 26 May 2017

A calsequestrin cis-regulatory motif coupled to a cardiac troponin T promoter improves cardiac AAV9 transduction specificity.

scientific article published on 15 March 2018

AAV Capsid Engineering: Zooming in on the Target

scientific article published in May 2017

Alteration of Cardiac Progenitor Cell Potency in GRMD Dogs

scientific article published in September 2012

Anti-viral strategies

scientific article published on January 1, 1995

Baboon envelope pseudotyped lentiviral vectors efficiently transduce human B cells and allow active factor IX B cell secretion in vivo in NOD/SCIDγc-/- mice.

scientific article published on 29 September 2016

Bone Marrow Stromal Cells as Targets for Gene Therapy of Hemophilia A

scientific article published on February 10, 1998

CRISPR/Cas9 Flexes Its Muscles: In Vivo Somatic Gene Editing for Muscular Dystrophy

scientific article

Clinical Progress in Gene Therapy: Sustained Partial Correction of the Bleeding Disorder in Patients Suffering from Severe Hemophilia B

scientific article published on January 1, 2012

Distinct transduction of muscle tissue in mice after systemic delivery of AAVpo1 vectors

scientific article published on 17 October 2019

Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells

scientific article published in September 2018

Gene and Cell Therapy: Tearing Down Walls

article

Gene therapy for hemophilia: hopes and hurdles

scientific article published on September 1, 1998

Gene therapy strategies for hemophilia: benefits versus risks

scientific article published on October 1, 2010

Genome-wide computational analysis reveals cardiomyocyte-specific transcriptional Cis-regulatory motifs that enable efficient cardiac gene therapy

scientific article published on 8 September 2014

Getting Into the Rhythm With CRISPR

scientific article published on 01 September 2018

HEMOPHILIA GENE THERAPY: READY FOR PRIME TIME?

scientific article published on 10 August 2017

Hyperactive piggyBac transposons for sustained and robust liver-targeted gene therapy

scientific article

Hyperfunctional coagulation factor IX improves the efficacy of gene therapy in hemophilic mice

scientific article

Identification of a myotropic AAV by massively parallel in vivo evaluation of barcoded capsid variants

scientific article published on 28 October 2020

Immunology of Gene and Cell Therapy

scientific article published on 04 February 2020

Moving forward toward a cure for hemophilia B.

scientific article published on May 2015

Next-generation muscle-directed gene therapy by in silico vector design

scientific article published in Nature Communications

Optimizing delivery and expression of designer nucleases for genome engineering

scientific article published on December 2013

PiggyBac Toolbox

scientific article published on January 1, 2012

Platelet‐directed gene therapy overcomes inhibitory antibodies to factor VIII

scientific article published on August 1, 2012

Preclinical and clinical advances in transposon-based gene therapy

scientific article published on 31 October 2017

Recent Progress in Gene Therapy for Hemophilia

scientific article published on June 1, 2012

Recent developments in transposon-mediated gene therapy

scientific article published on July 1, 2012

Retroviral Vectors Induce Epigenetic Chromatin Modifications and IL-10 Production in Transduced B Cells via Activation of Toll-like Receptor 2

scientific article published on December 14, 2010

Transposons: Moving Forward from Preclinical Studies to Clinical Trials.

scientific article published on 22 August 2017

Treatment of phenylketonuria using minicircle-based naked-DNA gene transfer to murine liver

scientific article published on 29 July 2014

Validation of miR-20a as a Tumor Suppressor Gene in Liver Carcinoma Using Hepatocyte-Specific Hyperactive piggyBac Transposons

scientific article published on 22 January 2020