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List of works by Michelle A Farrar

"Getting ready for the adult world": how adults with spinal muscular atrophy perceive and experience healthcare, transition and well-being

article

Great expectations: virus-mediated gene therapy in neurological disorders

scientific article published on 05 June 2020

Health, wellbeing and lived experiences of adults with SMA: a scoping systematic review

scientific article published on 12 March 2020

Inherited Paediatric Motor Neuron Disorders: Beyond Spinal Muscular Atrophy

scientific article

Motor unit changes in children with symptomatic spinal muscular atrophy treated with nusinersen

scientific article published on 26 October 2020

No gain - no pain? ⬇️

scientific article published on November 21, 2012

Restoration of Nusinersen Levels Following Treatment Interruption in People With Spinal Muscular Atrophy: Simulations Based on a Population Pharmacokinetic Model

scientific article published on 26 January 2022

Spinal muscular atrophy - the dawning of a new era

scientific article published on 25 September 2020

Treating adults with spinal muscular atrophy with nusinersen

scientific article published on 11 September 2020

Whole Genome Sequencing Identifies a 78 kb Insertion from Chromosome 8 as the Cause of Charcot-Marie-Tooth Neuropathy CMTX3.

scientific article

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