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List of works by Maria Candida Vila

Cell-Selective Adeno-Associated Virus-Mediated <i>SCN1A</i> Gene Regulation Therapy Rescues Mortality and Seizure Phenotypes in a Dravet Syndrome Mouse Model and Is Well Tolerated in Nonhuman Primates

scientific article published in 2022

Elusive sources of variability of dystrophin rescue by exon skipping

scientific article

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