Search filters

List of works by Lili Wang

A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice

scientific article published on February 2016

A factor IX-deficient mouse model for hemophilia B gene therapy

scientific article published on October 14, 1997

A mutation-independent CRISPR-Cas9-mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency

scientific article published on 12 February 2020

AAV gene therapy corrects OTC deficiency and prevents liver fibrosis in aged OTC-knock out heterozygous mice.

scientific article published on 2 March 2017

AAV8 induces tolerance in murine muscle as a result of poor APC transduction, T cell exhaustion, and minimal MHCI upregulation on target cells.

scientific article published on 19 June 2013

Adeno-associated Viral Vectors for Correction of Inborn Errors of Metabolism: Progressing Towards Clinical Application

scientific article published on January 1, 2011

Adeno-associated virus gene therapy prevents hepatocellular adenoma in murine model of glycogen storage disease type Ia

scientific article published on November 1, 2012

Adenovirus-mediated overexpression of follistatin enlarges intact liver of adult rats

scientific article published on November 1, 2003

Advances and challenges in adeno-associated viral inner-ear gene therapy for sensorineural hearing loss

scientific article published in 2021

CRISPR/Cas9-mediated in vivo gene targeting corrects hemostasis in newborn and adult factor IX-knockout mice

scientific article published on 11 April 2019

Chronic suppression of heart-failure progression by a pseudophosphorylated mutant of phospholamban via in vivo cardiac rAAV gene delivery

scientific article

Development and rescue of human familial hypercholesterolaemia in a xenograft mouse model

scientific article

Effects of Self-Complementarity, Codon Optimization, Transgene, and Dose on Liver Transduction with AAV8.

scientific article

Inhalation of nebulized perfluorochemical enhances recombinant adenovirus and adeno-associated virus-mediated gene expression in lung epithelium

scientific article

Robust Adenoviral and Adeno-Associated Viral Gene Transfer to the In Vivo Murine Heart

article