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List of works by Sonia M. Vallabh

Age of onset in genetic prion disease and the design of preventive clinical trials

Antisense oligonucleotides extend survival of prion-infected mice

scientific article published on 30 July 2019

Brainwide silencing of prion protein by AAV-mediated delivery of an engineered compact epigenetic editor

scientific article published on 28 June 2024

Characterization of the Prion Protein Binding Properties of Antisense Oligonucleotides

scientific article published on 18 December 2019

Disease stages and therapeutic hypotheses in two decades of neurodegenerative disease clinical trials

scientific article published in 2022

Domain-specific Quantification of Prion Protein in Cerebrospinal Fluid by Targeted Mass Spectrometry

scientific article published on 26 September 2019

Htt CAG repeat expansion confers pleiotropic gains of mutant huntingtin function in chromatin regulation

scientific article

Implications of new genetic risk factors in prion disease

scientific article published on 10 November 2020

Multimodal small-molecule screening for human prion protein binders

scientific article published on 28 July 2020

Prion protein lowering is a disease-modifying therapy across prion disease stages, strains and endpoints

scientific article published on 10 August 2020

Prion protein quantification in cerebrospinal fluid as a tool for prion disease drug development

article

Prion protein quantification in human cerebrospinal fluid as a tool for prion disease drug development

scientific article published on 01 April 2019

Quantifying prion disease penetrance using large population control cohorts

scientific article published on January 2016

Towards a treatment for genetic prion disease: trials and biomarkers

scientific article published on 18 March 2020

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