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List of works by Phillip A Doerfler

Activation of γ-globin gene expression by GATA1 and NF-Y in hereditary persistence of fetal hemoglobin

scientific article published on 02 August 2021

BAFF blockade prevents anti-drug antibody formation in a mouse model of Pompe disease

scientific article published on April 2015

Copackaged AAV9 Vectors Promote Simultaneous Immune Tolerance and Phenotypic Correction of Pompe Disease

scientific article published on 25 November 2015

Copackaging of multiple adeno-associated viral vectors in a single production step

scientific article published on 19 September 2014

Immune responses and hypercoagulation in ERT for Pompe disease are mutation and rhGAA dose dependent.

scientific article

Oral delivery of Acid Alpha Glucosidase epitopes expressed in plant chloroplasts suppresses antibody formation in treatment of Pompe mice

scientific article

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