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List of works by William Lostal

A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequence

scientific article

A naturally occurring human minidysferlin protein repairs sarcolemmal lesions in a mouse model of dysferlinopathy.

scientific article published in September 2010

Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies

scientific article published on 21 June 2016

Efficient recovery of dysferlin deficiency by dual adeno-associated vector-mediated gene transfer

scientific article published on 13 February 2010

Full-length dystrophin reconstitution with adeno-associated viral vectors

scientific article

Lack of correlation between outcomes of membrane repair assay and correction of dystrophic changes in experimental therapeutic strategy in dysferlinopathy

scientific article (publication date: 2012)

Titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy type 2A

scientific article published on 01 November 2019

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