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List of works by Elena Barbon

An engineered tale-transcription factor rescues transcription of factor VII impaired by promoter mutations and enhances its endogenous expression in hepatocytes

scientific article published on 24 June 2016

Molecular Basis and Therapeutic Strategies to Rescue Factor IX Variants That Affect Splicing and Protein Function

scientific article

Recombinant Adeno-Associated Viral Vectors Expressing Human Coagulation FIX-E456H Variant in Hemophilia B Mice

scientific article published on 28 October 2019

Regulation of a strong F9 cryptic 5'ss by intrinsic elements and by combination of tailored U1snRNAs with antisense oligonucleotides

scientific article published on 10 June 2015

Single-domain antibodies targeting antithrombin reduce bleeding in hemophilic mice with or without inhibitors

scientific article published on 11 March 2020

Tailoring the CRISPR system to transactivate coagulation gene promoters in normal and mutated contexts

scientific article published on 18 April 2019

Transposon-mediated Generation of Cellular and Mouse Models of Splicing Mutations to Assess the Efficacy of snRNA-based Therapeutics

scientific article published on 29 November 2016

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