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List of works by Xavier M Anguela

Adeno-associated viral vectors for the treatment of hemophilia.

scientific article published on 27 November 2015

An edible switch for gene therapy.

scientific article published in August 2016

Entering the Modern Era of Gene Therapy

scientific article published on 26 November 2018

Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.

scientific article published in December 2017

In vivo genome editing of the albumin locus as a platform for protein replacement therapy

scientific article

In vivo genome editing restores haemostasis in a mouse model of haemophilia

scientific article (publication date: 26 June 2011)

Molecular signature of the immune and tissue response to non-coding plasmid DNA in skeletal muscle after electrotransfer ⬇️

scientific article published on December 15, 2011

Overcoming preexisting humoral immunity to AAV using capsid decoys

scientific article published on July 2013

Preclinical evaluation of an anti-HCV miRNA cluster for treatment of HCV infection

scientific article published on 8 January 2013

Reversal of type 1 diabetes by engineering a glucose sensor in skeletal muscle.

scientific article published in June 2006

Robust ZFN-mediated genome editing in adult hemophilic mice.

scientific article published on October 2013

Skeletal muscle metabolism in the pathology and treatment of type 1 diabetes.

scientific article published on January 2010

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