List of works - Emmanuel Payen

Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.

scientific article published on January 2012

An activin receptor IIA ligand trap corrects ineffective erythropoiesis in β-thalassemia

scientific article

Arrayed lentiviral barcoding for quantification analysis of hematopoietic dynamics.

scientific article published in October 2013

Characterization of ovine SRY transcript and developmental expression of genes involved in sexual differentiation.

scientific article published on June 1996

Comparative HMG-box sequences of the SRY gene between sheep, cattle and goats

scientific article

Control of sex determination in animals.

scientific article

Correction of murine β-thalassemia after minimal lentiviral gene transfer and homeostatic in vivo erythroid expansion

scientific article

Current and future alternative therapies for beta-thalassemia major

scientific article

Distribution of lentiviral vector integration sites in mice following therapeutic gene transfer to treat β-thalassemia

scientific article

Enhanced Transduction of Macaca fascicularis Hematopoietic Cells with Chimeric Lentiviral Vectors

scientific article published on 15 May 2019

Evolutionary conservation of a microsatellite in the Wilms tumour (WT) gene: mapping in sheep and cattle.

scientific article published in January 1995

Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies

scientific article published on 24 October 2017

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

article

Gene Therapy in a Patient with Sickle Cell Disease

scientific article published on March 2017

Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene

scientific article published on February 2016

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

scientific article

Hemoglobin disorders: lentiviral gene therapy in the starting blocks to enter clinical practice

article

High-Efficiency Transduction of Primary Human Hematopoietic Stem/Progenitor Cells by AAV6 Vectors: Strategies for Overcoming Donor-Variation and Implications in Genome Editing.

scientific article published on 19 October 2016

Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles.

scientific article

Improvement of mouse beta-thalassemia by electrotransfer of erythropoietin cDNA.

scientific article published in March 2001

Innovative Therapies for Hemoglobin Disorders

scientific article published on 08 September 2020

Is normal hematopoiesis maintained solely by long-term multipotent stem cells?

scientific article

Lentivirus vectors in β-thalassemia.

scientific article published in January 2012

Long-term doxycycline-regulated secretion of erythropoietin by encapsulated myoblasts

scientific article

Nucleotide sequence of XLPOU3 cDNA, a member of the POU domain gene family expressed in Xenopus laevis embryos.

scientific article

Parallel assessment of globin lentiviral transfer in induced pluripotent stem cells and adult hematopoietic stem cells derived from the same transplanted β-thalassemia patient

scientific article published in September 2013

Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease

scientific article

Protective effects of phosphodiesterase-4 (PDE-4) inhibition in the early phase of pulmonary arterial hypertension in transgenic sickle cell mice

scientific article published on 01 February 2008

Sequence evolution of SRY gene within Bovidae family

article

Sheep gene mapping: assignment of ALDOB, CYP19, WT and SOX2 by somatic cell hybrid analysis.

scientific article

The Centromeric/Nucleolar Chromatin Protein ZFP-37 May Function to Specify Neuronal Nuclear Domains ⬇️

scientific article published on April 10, 1998

The genetics of sex

scientific article published on 01 June 1993

The ovine SOX2 gene: sequence, chromosomal localization and gonadal expression.

scientific article published on April 1997

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

scientific article

Transplantation of Macaca cynomolgus iPS-derived hematopoietic cells in NSG immunodeficient mice

scientific article published on 18 June 2015

List of works by Emmanuel Payen

Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.

An activin receptor IIA ligand trap corrects ineffective erythropoiesis in β-thalassemia

Arrayed lentiviral barcoding for quantification analysis of hematopoietic dynamics.

Characterization of ovine SRY transcript and developmental expression of genes involved in sexual differentiation.

Comparative HMG-box sequences of the SRY gene between sheep, cattle and goats

Control of sex determination in animals.

Correction of murine β-thalassemia after minimal lentiviral gene transfer and homeostatic in vivo erythroid expansion

Current and future alternative therapies for beta-thalassemia major

Distribution of lentiviral vector integration sites in mice following therapeutic gene transfer to treat β-thalassemia

Enhanced Transduction of Macaca fascicularis Hematopoietic Cells with Chimeric Lentiviral Vectors

Evolutionary conservation of a microsatellite in the Wilms tumour (WT) gene: mapping in sheep and cattle.

Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Gene Therapy in a Patient with Sickle Cell Disease

Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

Hemoglobin disorders: lentiviral gene therapy in the starting blocks to enter clinical practice

High-Efficiency Transduction of Primary Human Hematopoietic Stem/Progenitor Cells by AAV6 Vectors: Strategies for Overcoming Donor-Variation and Implications in Genome Editing.

Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles.

Improvement of mouse beta-thalassemia by electrotransfer of erythropoietin cDNA.

Innovative Therapies for Hemoglobin Disorders

Is normal hematopoiesis maintained solely by long-term multipotent stem cells?

Lentivirus vectors in β-thalassemia.

Long-term doxycycline-regulated secretion of erythropoietin by encapsulated myoblasts

Nucleotide sequence of XLPOU3 cDNA, a member of the POU domain gene family expressed in Xenopus laevis embryos.

Parallel assessment of globin lentiviral transfer in induced pluripotent stem cells and adult hematopoietic stem cells derived from the same transplanted β-thalassemia patient

Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease

Protective effects of phosphodiesterase-4 (PDE-4) inhibition in the early phase of pulmonary arterial hypertension in transgenic sickle cell mice

Sequence evolution of SRY gene within Bovidae family

Sheep gene mapping: assignment of ALDOB, CYP19, WT and SOX2 by somatic cell hybrid analysis.

The Centromeric/Nucleolar Chromatin Protein ZFP-37 May Function to Specify Neuronal Nuclear Domains ⬇️

The genetics of sex

The ovine SOX2 gene: sequence, chromosomal localization and gonadal expression.

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Transplantation of Macaca cynomolgus iPS-derived hematopoietic cells in NSG immunodeficient mice