List of works - Emmanuel Payen

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

scientific article

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

scientific article

Correction of Sickle Cell Disease in Transgenic Mouse Models by Gene Therapy

scientific article published on December 14, 2001

Gene Therapy in a Patient with Sickle Cell Disease

scientific article published on March 2017

An activin receptor IIA ligand trap corrects ineffective erythropoiesis in β-thalassemia

scientific article

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

article

Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease

scientific article

Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene

scientific article published on February 2016

Distribution of lentiviral vector integration sites in mice following therapeutic gene transfer to treat β-thalassemia

scientific article

Improvement of mouse beta-thalassemia by electrotransfer of erythropoietin cDNA.

scientific article published in March 2001

Is normal hematopoiesis maintained solely by long-term multipotent stem cells?

scientific article

Parallel assessment of globin lentiviral transfer in induced pluripotent stem cells and adult hematopoietic stem cells derived from the same transplanted β-thalassemia patient

scientific article published in September 2013

The Centromeric/Nucleolar Chromatin Protein ZFP-37 May Function to Specify Neuronal Nuclear Domains

scientific article published on April 10, 1998

Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.

scientific article published on January 2012

Correction of murine β-thalassemia after minimal lentiviral gene transfer and homeostatic in vivo erythroid expansion

scientific article

Long-term doxycycline-regulated secretion of erythropoietin by encapsulated myoblasts

scientific article

Protective effects of phosphodiesterase-4 (PDE-4) inhibition in the early phase of pulmonary arterial hypertension in transgenic sickle cell mice

scientific article published on 01 February 2008

Current and future alternative therapies for beta-thalassemia major

scientific article

Control of sex determination in animals.

scientific article published on 01 December 1993

Characterization of ovine SRY transcript and developmental expression of genes involved in sexual differentiation.

scientific article published on June 1996

Arrayed lentiviral barcoding for quantification analysis of hematopoietic dynamics.

scientific article published in October 2013

High-Efficiency Transduction of Primary Human Hematopoietic Stem/Progenitor Cells by AAV6 Vectors: Strategies for Overcoming Donor-Variation and Implications in Genome Editing.

scientific article published on 19 October 2016

Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles.

scientific article

Comparative HMG-box sequences of the SRY gene between sheep, cattle and goats

scientific article published on 01 June 1993

Nucleotide sequence of XLPOU3 cDNA, a member of the POU domain gene family expressed in Xenopus laevis embryos.

scientific article published on 01 April 1992

Lentivirus vectors in β-thalassemia.

scientific article published in January 2012

Sequence evolution of SRY gene within Bovidae family

article

Transplantation of Macaca cynomolgus iPS-derived hematopoietic cells in NSG immunodeficient mice

scientific article published on 18 June 2015

Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies

scientific article published on 24 October 2017

Sheep gene mapping: assignment of ALDOB, CYP19, WT and SOX2 by somatic cell hybrid analysis.

scientific article published on 01 October 1995

Hemoglobin disorders: lentiviral gene therapy in the starting blocks to enter clinical practice

article

The ovine SOX2 gene: sequence, chromosomal localization and gonadal expression.

scientific article published on April 1997

Evolutionary conservation of a microsatellite in the Wilms tumour (WT) gene: mapping in sheep and cattle.

scientific article published in January 1995

The genetics of sex

scientific article published on 01 June 1993

Innovative Therapies for Hemoglobin Disorders

scientific article published on 08 September 2020

Enhanced Transduction of Macaca fascicularis Hematopoietic Cells with Chimeric Lentiviral Vectors

scientific article published on 15 May 2019

List of works by Emmanuel Payen

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

Correction of Sickle Cell Disease in Transgenic Mouse Models by Gene Therapy

Gene Therapy in a Patient with Sickle Cell Disease

An activin receptor IIA ligand trap corrects ineffective erythropoiesis in β-thalassemia

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease

Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene

Distribution of lentiviral vector integration sites in mice following therapeutic gene transfer to treat β-thalassemia

Improvement of mouse beta-thalassemia by electrotransfer of erythropoietin cDNA.

Is normal hematopoiesis maintained solely by long-term multipotent stem cells?

Parallel assessment of globin lentiviral transfer in induced pluripotent stem cells and adult hematopoietic stem cells derived from the same transplanted β-thalassemia patient

The Centromeric/Nucleolar Chromatin Protein ZFP-37 May Function to Specify Neuronal Nuclear Domains

Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.

Correction of murine β-thalassemia after minimal lentiviral gene transfer and homeostatic in vivo erythroid expansion

Long-term doxycycline-regulated secretion of erythropoietin by encapsulated myoblasts

Protective effects of phosphodiesterase-4 (PDE-4) inhibition in the early phase of pulmonary arterial hypertension in transgenic sickle cell mice

Current and future alternative therapies for beta-thalassemia major

Control of sex determination in animals.

Characterization of ovine SRY transcript and developmental expression of genes involved in sexual differentiation.

Arrayed lentiviral barcoding for quantification analysis of hematopoietic dynamics.

High-Efficiency Transduction of Primary Human Hematopoietic Stem/Progenitor Cells by AAV6 Vectors: Strategies for Overcoming Donor-Variation and Implications in Genome Editing.

Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles.

Comparative HMG-box sequences of the SRY gene between sheep, cattle and goats

Nucleotide sequence of XLPOU3 cDNA, a member of the POU domain gene family expressed in Xenopus laevis embryos.

Lentivirus vectors in β-thalassemia.

Sequence evolution of SRY gene within Bovidae family

Transplantation of Macaca cynomolgus iPS-derived hematopoietic cells in NSG immunodeficient mice

Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies

Sheep gene mapping: assignment of ALDOB, CYP19, WT and SOX2 by somatic cell hybrid analysis.

Hemoglobin disorders: lentiviral gene therapy in the starting blocks to enter clinical practice

The ovine SOX2 gene: sequence, chromosomal localization and gonadal expression.

Evolutionary conservation of a microsatellite in the Wilms tumour (WT) gene: mapping in sheep and cattle.

The genetics of sex

Innovative Therapies for Hemoglobin Disorders

Enhanced Transduction of Macaca fascicularis Hematopoietic Cells with Chimeric Lentiviral Vectors