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List of works by Maria Grazia Roncarolo

79. Systemic Administration of Lentiviral Vectors Triggers Innate Host Responses

article

A CD4+ T-cell subset inhibits antigen-specific T-cell responses and prevents colitis

scientific article (publication date: 16 October 1997)

A hypomorphic R229Q Rag2 mouse mutant recapitulates human Omenn syndrome

scientific article published on May 2007

A novel function for FOXP3 in humans: intrinsic regulation of conventional T cells

scientific article

A novel human packaging cell line with hematopoietic supportive capacity increases gene transfer into early hematopoietic progenitors.

scientific article

A proportion of patients with lymphoma may harbor mutations of the perforin gene.

scientific article

A research institute at a turning point. Interview by Kathryn Claiborn

scientific article published on January 2012

ADA-deficient SCID is associated with a specific microenvironment and bone phenotype characterized by RANKL/OPG imbalance and osteoblast insufficiency

scientific article

APVO210: A Bispecific Anti-CD86-IL-10 Fusion Protein (ADAPTIR™) to Induce Antigen-Specific T Regulatory Type 1 Cells.

scientific article published on 25 May 2018

Abnormalities of acid-base balance and predisposition to metabolic acidosis in Metachromatic Leukodystrophy patients

scientific article published on 6 March 2015

Absence of VOD in paediatric thalassaemic HSCT recipients using defibrotide prophylaxis and intravenous Busulphan.

scientific article published on 31 August 2009

Activation of the aryl hydrocarbon receptor promotes allograft-specific tolerance through direct and dendritic cell-mediated effects on regulatory T cells

scientific article published on 11 June 2008

Activation-induced FOXP3 in human T effector cells does not suppress proliferation or cytokine production

scientific article published on 27 February 2007

Administration of Flk2/Flt3 ligand induces expansion of human high-proliferative potential colony-forming cells in the SCID-hu mouse

scientific article published on 01 June 1999

Alterations in the adenosine metabolism and CD39/CD73 adenosinergic machinery cause loss of Treg cell function and autoimmunity in ADA-deficient SCID

scientific article

Altered intracellular and extracellular signaling leads to impaired T-cell functions in ADA-SCID patients

scientific article published on 24 January 2008

An anti-CD45RO/RB monoclonal antibody modulates T cell responses via induction of apoptosis and generation of regulatory T cells.

scientific article

Analysis of galactocerebrosidase activity in the mouse brain by a new histological staining method.

scientific article published in August 2004

Antigen-specific dependence of Tr1-cell therapy in preclinical models of islet transplant

scientific article

Author Correction: Gene correction for SCID-X1 in long-term hematopoietic stem cells

article

Author Correction: Gene correction for SCID-X1 in long-term hematopoietic stem cells

scientific article published on 04 December 2019

Autoimmune diabetic patients undergoing allogeneic islet transplantation: are we ready for a regulatory T-cell therapy?

scientific article published on 28 July 2009

B-cell development and functions and therapeutic options in adenosine deaminase-deficient patients.

scientific article published on 5 February 2014

B-cell reconstitution after lentiviral vector-mediated gene therapy in patients with Wiskott-Aldrich syndrome.

scientific article published on 16 March 2015

BAT2 and BAT3 polymorphisms as novel genetic risk factors for rejection after HLA-related SCT

scientific article

Beneficial autoimmunity in Type 1 diabetes mellitus

scientific article

Bone marrow as a source of hematopoietic stem cells for human gene therapy of β-thalassemia

scientific article published on March 4, 2011

CD4+ T-regulatory cells: toward therapy for human diseases.

scientific article published on June 2008

CD4+ regulatory T cells: mechanisms of induction and effector function.

scientific article

CD4⁺ T cells from IPEX patients convert into functional and stable regulatory T cells by FOXP3 gene transfer

scientific article published on December 2013

Celebrating 20 years of FOCIS

scientific article published on 01 October 2020

Characterization of new arylsulfatase A gene mutations reinforces genotype-phenotype correlation in metachromatic leukodystrophy.

scientific article

Clinical and molecular profile of a new series of patients with immune dysregulation, polyendocrinopathy, enteropathy, X-linked syndrome: inconsistent correlation between forkhead box protein 3 expression and disease severity.

scientific article published on 25 October 2008

Clinical improvement and normalized Th1 cytokine profile in early and long-term interferon-alpha treatment in a suspected case of hyper-IgE syndrome

scientific article

Coexpression of CD163 and CD141 identifies human circulating IL-10-producing dendritic cells (DC-10)

scientific article published on 06 March 2019

Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning

scientific article published in June 2002

Correction of beta-thalassemia major by gene transfer in haematopoietic progenitors of pediatric patients.

scientific article

Corrigendum to "Evidence for Long-term Efficacy and Safety of Gene Therapy for Wiskott-Aldrich Syndrome in Preclinical Models".

scientific article published on July 2009

Current understanding of the Wiskott-Aldrich syndrome and prospects for gene therapy.

scientific article

Defective regulatory and effector T cell functions in patients with FOXP3 mutations.

scientific article

Demethylation analysis of the FOXP3 locus shows quantitative defects of regulatory T cells in IPEX-like syndrome.

scientific article published on 20 January 2012

Dendritic cell functional improvement in a preclinical model of lentiviral-mediated gene therapy for Wiskott-Aldrich syndrome

scientific article

Design and optimization of lentiviral vectors for transfer of GALC expression in Twitcher brain.

scientific article published in August 2006

Differentiation of Tr1 cells by immature dendritic cells requires IL-10 but not CD25+CD4+ Tr cells

scientific article

Differentiation of type 1 T regulatory cells (Tr1) by tolerogenic DC-10 requires the IL-10-dependent ILT4/HLA-G pathway

scientific article

Do human TH1 and TH2 CD4+ clones exist? ⬇️

scientific article published on January 1, 1991

Driving Medical Innovation Through Interdisciplinarity: Unique Opportunities and Challenges

article

Efficacy of gene therapy for Wiskott-Aldrich syndrome using a WAS promoter/cDNA-containing lentiviral vector and nonlethal irradiation.

scientific article published in March 2006

Efficient gene transfer into primitive hematopoietic progenitors using a bone marrow microenvironment cell line engineered to produce retroviral vectors.

scientific article published on April 2004

Enforced IL-10 expression confers type 1 regulatory T cell (Tr1) phenotype and function to human CD4(+) T cells.

scientific article

Engineered T Regulatory Type 1 Cells for Clinical Application.

scientific article published on 15 February 2018

Engineered type 1 regulatory T cells designed for clinical use kill primary pediatric acute myeloid leukemia cells

scientific article published on 28 September 2020

Escalating doses of donor lymphocytes for incipient graft rejection following SCT for thalassemia.

scientific article

Evidence for long-term efficacy and safety of gene therapy for Wiskott-Aldrich syndrome in preclinical models

scientific article

Ex vivo gene therapy with lentiviral vectors rescues adenosine deaminase (ADA)-deficient mice and corrects their immune and metabolic defects

scientific article published on 11 July 2006

F.75. Molecular and Functional Studies in T Cells from Healthy Carriers of FOXP3 Mutations

scholarly article by Rosa Bacchetta et al published January 2008 in Clinical Immunology

Fatal autoimmunity in mice reconstituted with human hematopoietic stem cells encoding defective FOXP3

scientific article published on April 2015

Fatal vancomycin- and linezolid-resistant Enterococcus faecium sepsis in a child undergoing allogeneic haematopoietic stem cell transplantation for beta-thalassaemia major.

scientific article published on 18 March 2010

First Occurrence of Plasmablastic Lymphoma in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Disease Patient and Review of the Literature.

scientific article published on 2 February 2018

Forkhead box P3: the peacekeeper of the immune system.

scientific article published on 19 December 2013

Forkhead box protein 3 (FOXP3) mutations lead to increased TH17 cell numbers and regulatory T-cell instability

scientific article published on 13 October 2011

Frequency and targeted detection of HLA-DPB1 T cell epitope disparities relevant in unrelated hematopoietic stem cell transplantation.

scientific article published on 20 July 2007

Functional type 1 regulatory T cells develop regardless of FOXP3 mutations in patients with IPEX syndrome.

scientific article published on 14 March 2011

Gene Therapy

scientific article published on 01 August 2019

Gene Therapy for Adenosine Deaminase Deficiency: A Comprehensive Evaluation of Short- and Medium-Term Safety

scientific article published on 4 January 2018

Gene Therapy for Wiskott-Aldrich Syndrome: History, New Vectors, Future Directions

scientific article published on 02 July 2020

Gene correction for SCID-X1 in long-term hematopoietic stem cells

article

Gene therapy for ADA-SCID, the first marketing approval of an ex vivo gene therapy in Europe: paving the road for the next generation of advanced therapy medicinal products

scientific article

Gene therapy for adenosine deaminase deficiency

scientific article published in December 2003

Gene therapy for immunodeficiency due to adenosine deaminase deficiency.

scientific article

Gene therapy for primary immunodeficiency

scientific article published on 01 October 2019

Generation of potent and stable human CD4+ T regulatory cells by activation-independent expression of FOXP3.

scientific article published on 6 November 2007

Generation of primary antigen-specific human T- and B-cell responses in immunocompetent SCID-hu mice

scientific article published on 01 January 2000

Genome editing of donor-derived T-cells to generate allogenic chimeric antigen receptor-modified T cells: Optimizing αβ T cell-depleted haploidentical hematopoietic stem cell transplantation

scientific article published on 02 April 2020

Graft Engineering and Adoptive Immunotherapy: New Approaches to Promote Immune Tolerance After Hematopoietic Stem Cell Transplantation

scientific article published on 10 July 2019

Granulocyte-colony stimulating factor drives the in vitro differentiation of human dendritic cells that induce anergy in naïve T cells

scientific article

HIV-1-derived lentiviral vectors directly activate plasmacytoid dendritic cells, which in turn induce the maturation of myeloid dendritic cells.

scientific article

HLA-G expressing DC-10 and CD4(+) T cells accumulate in human decidua during pregnancy

scientific article published on 10 December 2012

HLA-G expression levels influence the tolerogenic activity of human DC-10.

scientific article published on 6 February 2015

Health related quality of life in Middle Eastern children with beta-thalassemia

scientific article

Hematopoietic stem cell gene therapy for adenosine deaminase deficient-SCID.

scientific article

Hepatocyte-targeted expression by integrase-defective lentiviral vectors induces antigen-specific tolerance in mice with low genotoxic risk

scientific article

High incidence of severe cyclosporine neurotoxicity in children affected by haemoglobinopaties undergoing myeloablative haematopoietic stem cell transplantation: early diagnosis and prompt intervention ameliorates neurological outcome

scientific article

Human CD25+CD4+ T suppressor cell clones produce transforming growth factor beta, but not interleukin 10, and are distinct from type 1 T regulatory cells.

scientific article

Human CD4+ regulatory T cells and activation-induced tolerance.

scientific article

Human IL2RA null mutation mediates immunodeficiency with lymphoproliferation and autoimmunity

scientific article

Human T-and B-cell functions in SCID-hu mice.

scientific article published on August 1996

Human cd25(+)cd4(+) t regulatory cells suppress naive and memory T cell proliferation and can be expanded in vitro without loss of function.

scientific article published in June 2001

Hurdles in therapy with regulatory T cells

scientific article published on September 2015

IL-10 and TGF-beta induce alloreactive CD4+CD25- T cells to acquire regulatory cell function

scientific article published on 27 February 2003

IL-10-Engineered Human CD4(+) Tr1 Cells Eliminate Myeloid Leukemia in an HLA Class I-Dependent Mechanism.

scientific article published on 5 July 2017

IL-3 or IL-7 increases ex vivo gene transfer efficiency in ADA-SCID BM CD34+ cells while maintaining in vivo lymphoid potential.

scientific article published in December 2004

Identification of a common T/natural killer cell progenitor in human fetal thymus.

scientific article published on August 1994

Immune intervention with T regulatory cells: past lessons and future perspectives for type 1 diabetes.

scientific article published on June 2011

Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement

scientific article published in May 2002

Immune responses in liver-directed lentiviral gene therapy.

scientific article published on 26 January 2013

Immunological Outcome in Haploidentical-HSC Transplanted Patients Treated with IL-10-Anergized Donor T Cells

scientific article published on 31 January 2014

Immunological lessons learnt from patients transplanted with fully mismatched stem cells

scientific article published on 01 January 2007

Immunological tolerance following stem cell transplantation in human fetuses in utero ⬇️

scientific article published on 01 August 1997

In vivo T-cell dynamics during immune reconstitution after hematopoietic stem cell gene therapy in adenosine deaminase severe combined immune deficiency ⬇️

scientific article published on April 7, 2011

In vivo administration of lentiviral vectors triggers a type I interferon response that restricts hepatocyte gene transfer and promotes vector clearance.

scientific article published in April 2007

In vivo tracking of T cells in humans unveils decade-long survival and activity of genetically modified T memory stem cells

scientific article published on February 2015

In-utero transplantation of stem cells in bare lymphocyte syndrome.

scientific article

Inducing and Enhancing Effects of IL-3, -5, and -6 and GM-CSF on Histamine Release from Human Basophils ⬇️

scientific article published on 01 June 1993

Induction of anergic allergen-specific suppressor T cells using tolerogenic dendritic cells derived from children with allergies to house dust mites.

scientific article published on 11 February 2010

Induction of tolerance in type 1 diabetes via both CD4+CD25+ T regulatory cells and T regulatory type 1 cells

scientific article published in June 2006

Induction of transplantation tolerance in humans using fetal cell transplants

scientific article published on 01 January 2005

Induction of transplantation tolerance via regulatory T cells.

scientific article published on September 2006

InsB9-23 Gene Transfer To Hepatocytes-Based Combined Therapy Abrogates Recurrence of Type-1 Diabetes After Islet Transplantation

scientific article published on 29 October 2020

Insulin B chain 9-23 gene transfer to hepatocytes protects from type 1 diabetes by inducing Ag-specific FoxP3+ Tregs.

scientific article

Integration of retroviral vectors induces minor changes in the transcriptional activity of T cells from ADA-SCID patients treated with gene therapy.

scientific article

Integration profile of retroviral vector in gene therapy treated patients is cell-specific according to gene expression and chromatin conformation of target cell

scientific article

Interleukin-10-secreting type 1 regulatory T cells in rodents and humans.

scientific article

Interleukin-2 production and interleukin-2 receptor expression in children with newly diagnosed diabetes

article

In Vivo Tracking of Human Hematopoiesis Reveals Patterns of Clonal Dynamics during Early and Steady-State Reconstitution Phases

scientific article published on 25 May 2016

Isolation, Expansion, and Characterization of Human Natural and Adaptive Regulatory T Cells

Isolation, expansion, and characterization of human natural and adaptive regulatory T cells

scientific article published on January 2007

Killing of myeloid APCs via HLA class I, CD2 and CD226 defines a novel mechanism of suppression by human Tr1 cells.

scientific article published on 13 May 2011

Lentiviral Gene Therapy in HSCs Restores Lineage-Specific Foxp3 Expression and Suppresses Autoimmunity in a Mouse Model of IPEX Syndrome

scientific article published on 10 January 2019

Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial.

scientific article published on 8 June 2016

Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study

article

Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy

scientific article

Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome.

scientific article

Lentiviral vector-mediated gene transfer in T cells from Wiskott-Aldrich syndrome patients leads to functional correction.

scientific article

Lentiviral vectors targeting WASp expression to hematopoietic cells, efficiently transduce and correct cells from WAS patients.

scientific article published on 19 October 2006

Lentiviral-mediated gene therapy leads to improvement of B-cell functionality in a murine model of Wiskott-Aldrich syndrome

scientific article

Liver gene therapy by lentiviral vectors reverses anti-factor IX pre-existing immunity in haemophilic mice

scientific article published on 16 September 2013

Loss of mismatched HLA in leukemia after stem-cell transplantation.

scientific article

Lymphoid and myeloid differentiation of fetal liver CD34+lineage- cells in human thymic organ culture.

scientific article

Manipulating Immune Tolerance with Micro-RNA Regulated Gene Therapy.

scientific article

Methods for in vitro generation of human type 1 regulatory T cells

scientific article published in January 2011

Minimum Information about T Regulatory Cells: A Step toward Reproducibility and Standardization

scientific article published in January 2017

Mobilized blood CD34+ cells transduced and selected with a clinically applicable protocol reconstitute lymphopoiesis in SCID-Hu mice.

scientific article published in March 2004

Molecular Regulation ofCellular Immunity by FOXP3

Molecular and functional characterization of allogantigen-specific anergic T cells suitable for cell therapy.

scientific article published on 16 August 2010

Molecular and functional heterogeneity of IL-10-producing CD4 T cells

scientific article published in Nature Communications

Molecular purging of multiple myeloma cells by ex-vivo culture and retroviral transduction of mobilized-blood CD34+ cells

scientific article

Molecular regulation of cellular immunity by FOXP3.

scientific article published on January 2009

Multilineage hematopoietic reconstitution without clonal selection in ADA-SCID patients treated with stem cell gene therapy

scientific article published in August 2007

Multiple BM harvests in pediatric donors for thalassemic siblings: safety, efficacy and ethical issues

scientific article published on 23 June 2008

OR.40. Foxp3 Mutations in Children: Different Degrees of Impairment in Regulatory and Effector T-Cell Functions in Patients with Distinct Genotypes and Phenotypes

Peanut-specific type 1 regulatory T cells induced in vitro from allergic subjects are functionally impaired.

scientific article published on 6 July 2017

Platelet transfusion refractoriness in highly immunized beta thalassemia children undergoing stem cell transplantation

scientific article published on 07 January 2010

Point mutants of forkhead box P3 that cause immune dysregulation, polyendocrinopathy, enteropathy, X-linked have diverse abilities to reprogram T cells into regulatory T cells

scientific article published on 30 October 2010

Preclinical safety and efficacy of human CD34(+) cells transduced with lentiviral vector for the treatment of Wiskott-Aldrich syndrome

scientific article

Progress in the ex vivo expansion of hematopoietic progenitors.

scientific article

Prospective assessment of health-related quality of life in pediatric patients with beta-thalassemia following hematopoietic stem cell transplantation

scientific article published on 24 September 2010

Rapamycin and interleukin-10 treatment induces T regulatory type 1 cells that mediate antigen-specific transplantation tolerance.

scientific article published in January 2006

Rapamycin combined with anti-CD45RB mAb and IL-10 or with G-CSF induces tolerance in a stringent mouse model of islet transplantation

scientific article (publication date: 2011)

Rapamycin monotherapy in patients with type 1 diabetes modifies CD4+CD25+FOXP3+ regulatory T-cells

scientific article published on 16 June 2008

Rapamycin selectively expands CD4+CD25+FoxP3+ regulatory T cells.

scientific article published on 3 March 2005

Recent advances in understanding the pathophysiology of Wiskott-Aldrich syndrome

scientific article

Recombinant human interleukin 10 suppresses gliadin dependent T cell activation in ex vivo cultured coeliac intestinal mucosa.

scientific article

Regulatory T cells: prospective for clinical application in hematopoietic stem cell transplantation.

scientific article

Regulatory T cells: recommendations to simplify the nomenclature.

scientific article published in April 2013

Regulatory T-cell immunotherapy for tolerance to self antigens and alloantigens in humans.

scientific article published on August 2007

Reply to Comment on “Stability of human rapamycin-expanded CD4+CD25+ T-regulatory cells” Haematologica 2011;96(9):1357–65.

scientific article published in May 2012

Reprogramming human T cell function and specificity with non-viral genome targeting

Reprogramming human T cell function and specificity with non-viral genome targeting

scientific article published in Nature

Revertant T lymphocytes in a patient with Wiskott-Aldrich syndrome: analysis of function and distribution in lymphoid organs.

scientific article

Role of human FOXP3 in early thymic maturation and peripheral T cell homeostasis.

scientific article published on 26 April 2018

Role of human leukocyte antigen-G in the induction of adaptive type 1 regulatory T cells.

scientific article published on 04 August 2009

Role of reduced intensity conditioning in T-cell and B-cell immune reconstitution after HLA-identical bone marrow transplantation in ADA-SCID.

scientific article published on 11 May 2010

Role of regulatory T cells and FOXP3 in human diseases.

scientific article

SAP controls the cytolytic activity of CD8+ T cells against EBV-infected cells.

scientific article

STAT5-signaling cytokines regulate the expression of FOXP3 in CD4+CD25+ regulatory T cells and CD4+CD25- effector T cells.

scientific article published on 12 February 2008

Second hematopoietic SCT in patients with thalassemia recurrence following rejection of the first graft

scientific article published on 23 June 2008

Sirolimus-based graft-versus-host disease prophylaxis promotes the in vivo expansion of regulatory T cells and permits peripheral blood stem cell transplantation from haploidentical donors.

scientific article published on 4 June 2014

Stability of human rapamycin-expanded CD4+CD25+ T regulatory cells

scientific article

Su.98. Defining a Role for FOXP3 in Human Cd4+ T-Cells

T lymphocytes from human chimeras do recognize antigen in the context of allogeneic determinants of the major histocompatibility complex

scientific article published on 01 December 1993

Targeting lentiviral vector expression to hepatocytes limits transgene-specific immune response and establishes long-term expression of human antihemophilic factor IX in mice

scientific article

Temporal, quantitative, and functional characteristics of single-KIR-positive alloreactive natural killer cell recovery account for impaired graft-versus-leukemia activity after haploidentical hematopoietic stem cell transplantation.

scientific article

Ten years of gene therapy for primary immune deficiencies.

scientific article published on January 2009

Th17 cells express interleukin-10 receptor and are controlled by Foxp3⁻ and Foxp3+ regulatory CD4+ T cells in an interleukin-10-dependent manner

scientific article

The Biology of T Regulatory Type 1 Cells and Their Therapeutic Application in Immune-Mediated Diseases

scientific article published on 01 December 2018

The Cellular and Molecular Mechanisms of Immuno-Suppression by Human Type 1 Regulatory T Cells ⬇️

scientific article published on February 29, 2012

The Tregs' world according to GARP.

scientific article published in December 2009

The Wiskott-Aldrich syndrome protein is required for iNKT cell maturation and function.

scientific article published on 23 March 2009

The X-linked lymphoproliferative-disease gene product SAP regulates signals induced through the co-receptor SLAM ⬇️

scientific article published on October 1, 1998

The fate of human Treg cells.

scientific article

The immune response to lentiviral-delivered transgene is modulated in vivo by transgene-expressing antigen-presenting cells but not by CD4+CD25+ regulatory T cells.

scientific article published on 10 May 2007

The puzzling world of murine T regulatory cells.

scientific article

The role of 2 FOXP3 isoforms in the generation of human CD4+ Tregs.

scientific article published on 6 October 2005

The role of IL-10 and TGF-beta in the differentiation and effector function of T regulatory cells

scientific article

The role of interleukin 10 in the control of autoimmunity.

scientific article

The role of tissue adaptation and graft size in immune tolerance.

scientific article published on 15 June 2007

Therapeutic applications for hematopoietic stem cell gene transfer

scientific article

Tr1 cells and the counter-regulation of immunity: natural mechanisms and therapeutic applications.

scientific article published on January 2014

Tr1 cells: from discovery to their clinical application.

scientific article

Transgene expression of bcl-xL permits anti-immunoglobulin (Ig)-induced proliferation in xid B cells

scientific article

Transplant tolerance to pancreatic islets is initiated in the graft and sustained in the spleen

scientific article published on 8 July 2013

Treatment of X-linked severe combined immunodeficiency by in utero transplantation of paternal bone marrow

scientific article published on 01 December 1996

Treatment with rapamycin can restore regulatory T-cell function in IPEX patients

scientific article published on 23 December 2019

Tregopathies: Monogenic diseases resulting in regulatory T-cell deficiency

scientific article published on 01 December 2018

Type 1 T Regulatory Cells and Their Relationship with CD4+ CD25+ T Regulatory Cells

Type 1 T regulatory cells and their relationship with CD4+CD25+ T regulatory cells

scientific article published on January 1, 2003

Type 1 T regulatory cells.

scientific article

Type 1 regulatory T (Tr1) cells: from the bench to the bedside

scientific article published on 28 November 2012

Type 1 regulatory T cells are associated with persistent split erythroid/lymphoid chimerism after allogeneic hematopoietic stem cell transplantation for thalassemia.

scientific article published on 16 July 2009

Unpredictability of intravenous busulfan pharmacokinetics in children undergoing hematopoietic stem cell transplantation for advanced beta thalassemia: limited toxicity with a dose-adjustment policy.

scientific article published on 4 December 2009

Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency.

scientific article published on 29 April 2016

Utilizing regulatory T cells to control alloreactivity.

scientific article

Wild-type FOXP3 is selectively active in CD4+CD25(hi) regulatory T cells of healthy female carriers of different FOXP3 mutations

scientific article

Wiskott-Aldrich syndrome protein regulates lipid raft dynamics during immunological synapse formation.

scientific article published in August 2002

[Biomedical research: a need or a luxury?]

scientific article published on 01 March 2008

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