List of works - Andrea Calabria

A multilevel data integration resource for breast cancer study

scientific article

Assessing the Impact of Cyclosporin A on Lentiviral Transduction and Preservation of Human Hematopoietic Stem Cells in Clinically Relevant Ex Vivo Gene Therapy Settings

scientific article published on 24 May 2019

Genomewide association study using a high-density single nucleotide polymorphism array and case-control design identifies a novel essential hypertension susceptibility locus in the promoter region of endothelial NO synthase

scientific article published on 19 December 2011

Grid Based Genome Wide Studies on Atrial Flutter

HIV-1-mediated insertional activation of STAT5B and BACH2 trigger viral reservoir in T regulatory cells.

scientific article published on 8 September 2017

Immunotherapy of acute leukemia by chimeric antigen receptor-modified lymphocytes using an improved Sleeping Beauty transposon platform

scientific article published on 13 June 2016

In vivo tracking of T cells in humans unveils decade-long survival and activity of genetically modified T memory stem cells

scientific article published on February 2015

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

article

Intrathymic adeno-associated virus gene transfer rapidly restores thymic function and long-term persistence of gene-corrected T cells

scientific article published on 09 September 2019

Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial.

scientific article published on 8 June 2016

Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy

scientific article

Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome.

scientific article

Lentiviral vector-based insertional mutagenesis identifies genes involved in the resistance to targeted anticancer therapies

scientific article published on 8 September 2014

MYO1E mutations and childhood familial focal segmental glomerulosclerosis

scientific article

Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia

article

Ontological Enrichment of the Genes-to-Systems Breast Cancer Database

article

Ontology-based resources for bioinformatics analysis

Pervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe-affected non-human primates by intracerebral lentiviral gene therapy

scientific article published on 29 March 2016

Phagocytosis-shielded lentiviral vectors improve liver gene therapy in nonhuman primates

scientific article published on 01 May 2019

Precise Gene Editing Preserves Hematopoietic Stem Cell Function following Transient p53-Mediated DNA Damage Response

article

Preclinical testing of the safety and tolerability of LV-mediated above normal alpha-L-iduronidase expression in murine and human hematopoietic cells using toxicology and biodistribution GLP studies

scientific article published on 18 July 2016

SNPranker 2.0: a gene-centric data mining tool for diseases associated SNP prioritization in GWAS ⬇️

scientific article published on January 14, 2013

Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency

scientific article

Targeted genome editing in human repopulating haematopoietic stem cells

scientific article published on 28 May 2014

Targeted next-generation sequencing appoints c16orf57 as clericuzio-type poikiloderma with neutropenia gene

scientific article

VISPA2: a scalable pipeline for high-throughput identification and annotation of vector integration sites

scientific article published on 25 November 2017

VISPA: a computational pipeline for the identification and analysis of genomic vector integration sites

scientific article published on 3 September 2014

adLIMS: a customized open source software that allows bridging clinical and basic molecular research studies

scientific article published on June 2015

miRNA-126 Orchestrates an Oncogenic Program in B Cell Precursor Acute Lymphoblastic Leukemia

scientific article published in June 2016

List of works by Andrea Calabria

A multilevel data integration resource for breast cancer study

Assessing the Impact of Cyclosporin A on Lentiviral Transduction and Preservation of Human Hematopoietic Stem Cells in Clinically Relevant Ex Vivo Gene Therapy Settings

Genomewide association study using a high-density single nucleotide polymorphism array and case-control design identifies a novel essential hypertension susceptibility locus in the promoter region of endothelial NO synthase

Grid Based Genome Wide Studies on Atrial Flutter

HIV-1-mediated insertional activation of STAT5B and BACH2 trigger viral reservoir in T regulatory cells.

Immunotherapy of acute leukemia by chimeric antigen receptor-modified lymphocytes using an improved Sleeping Beauty transposon platform

In vivo tracking of T cells in humans unveils decade-long survival and activity of genetically modified T memory stem cells

Intrabone hematopoietic stem cell gene therapy for adult and pediatric patients affected by transfusion-dependent ß-thalassemia

Intrathymic adeno-associated virus gene transfer rapidly restores thymic function and long-term persistence of gene-corrected T cells

Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial.

Lentiviral hematopoietic stem cell gene therapy benefits metachromatic leukodystrophy

Lentiviral hematopoietic stem cell gene therapy in patients with Wiskott-Aldrich syndrome.

Lentiviral vector-based insertional mutagenesis identifies genes involved in the resistance to targeted anticancer therapies

MYO1E mutations and childhood familial focal segmental glomerulosclerosis

Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia

Ontological Enrichment of the Genes-to-Systems Breast Cancer Database

Ontology-based resources for bioinformatics analysis

Pervasive supply of therapeutic lysosomal enzymes in the CNS of normal and Krabbe-affected non-human primates by intracerebral lentiviral gene therapy

Phagocytosis-shielded lentiviral vectors improve liver gene therapy in nonhuman primates

Precise Gene Editing Preserves Hematopoietic Stem Cell Function following Transient p53-Mediated DNA Damage Response

Preclinical testing of the safety and tolerability of LV-mediated above normal alpha-L-iduronidase expression in murine and human hematopoietic cells using toxicology and biodistribution GLP studies

SNPranker 2.0: a gene-centric data mining tool for diseases associated SNP prioritization in GWAS ⬇️

Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency

Targeted genome editing in human repopulating haematopoietic stem cells

Targeted next-generation sequencing appoints c16orf57 as clericuzio-type poikiloderma with neutropenia gene

VISPA2: a scalable pipeline for high-throughput identification and annotation of vector integration sites

VISPA: a computational pipeline for the identification and analysis of genomic vector integration sites

adLIMS: a customized open source software that allows bridging clinical and basic molecular research studies

miRNA-126 Orchestrates an Oncogenic Program in B Cell Precursor Acute Lymphoblastic Leukemia