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List of works by Annarita Miccio

An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype

scientific article published on 04 August 2018

Base-editing-mediated dissection of a γ-globin cis-regulatory element for the therapeutic reactivation of fetal hemoglobin expression

scientific article published on 4 November 2022

CoCas9 is a compact nuclease from the human microbiome for efficient and precise genome editing

scientific article published in 2024

Concise Review: Epigenetic Regulation of Hematopoiesis: Biological Insights and Therapeutic Applications

scientific article published on 28 October 2017

Deletion of the LTR enhancer/promoter has no impact on the integration profile of MLV vectors in human hematopoietic progenitors

scientific article

Dynamic Transcriptional and Epigenetic Regulation of Human Epidermal Keratinocyte Differentiation.

scientific article published on 23 March 2016

Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype

scientific article published on 12 February 2020

GATA Factor-Mediated Gene Regulation in Human Erythropoiesis

scientific article published on 30 March 2020

GATA factor transcriptional activity: Insights from genome-wide binding profiles

scientific article published on 01 October 2019

Gene Therapy for β-Hemoglobinopathies

scientific article

Gene therapy targeting haematopoietic stem cells for inherited diseases: progress and challenges

scientific article published on 01 June 2019

Genome-Wide Definition of Promoter and Enhancer Usage during Neural Induction of Human Embryonic Stem Cells.

scientific article published on 15 May 2015

Genome-wide analysis of promoter and enhancer usage in hematopoietic stem cell differentiation

scientific article

Hot spots of retroviral integration in human CD34+ hematopoietic cells

scientific article

Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human β-globin locus.

scientific article published on 8 March 2018

Lentiviral and genome-editing strategies for the treatment of β-hemoglobinopathies

scientific article published on 01 October 2019

Lentiviral vector integration in the human genome induces alternative splicing and generates aberrant transcripts

scientific article

NuRD mediates activating and repressive functions of GATA-1 and FOG-1 during blood development

scientific article published on 19 November 2009

Nup153 and Nup98 bind the HIV-1 core and contribute to the early steps of HIV-1 replication

article

Nup153 and Nup98 bind the HIV-1 core and contribute to the early steps of HIV-1 replication.

scientific article published on 21 March 2013

Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements

scientific article published on 17 October 2018

Phosphorylation of synapsin I by cAMP-dependent protein kinase controls synaptic vesicle dynamics in developing neurons

scientific article published on 01 August 2005

Plerixafor enables the safe, rapid, efficient mobilization of haematopoietic stem cells in sickle cell disease patients after exchange transfusion

scientific article published on 22 February 2018

Retroviral Scanning: Mapping MLV Integration Sites to Define Cell-specific Regulatory Regions

scientific article

Role of the GATA-1/FOG-1/NuRD pathway in the expression of human beta-like globin genes.

scientific article

The GATA1-HS2 enhancer allows persistent and position-independent expression of a β-globin transgene

scientific article

The homeodomain transcription factor Prep1 (pKnox1) is required for hematopoietic stem and progenitor cell activity

scientific journal article

Transcription factor binding sites are genetic determinants of retroviral integration in the human genome

scientific article

Transcriptional, epigenetic and retroviral signatures identify regulatory regions involved in hematopoietic lineage commitment.

scientific article published on 20 April 2016

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