List of works - Adeline A. Lau

A Preclinical Study Evaluating AAVrh10-Based Gene Therapy for Sanfilippo Syndrome

scientific article

A novel conditional Sgsh knockout mouse model recapitulates phenotypic and neuropathic deficits of Sanfilippo syndrome

scientific article published on 27 April 2017

A simple method for early age phenotype confirmation using toe tissue from a mouse model of MPS IIIA

scientific article published on 01 April 2014

AAVrh10 Vector Corrects Disease Pathology in MPS IIIA Mice and Achieves Widespread Distribution of SGSH in Large Animal Brains

scientific article published on 10 December 2019

Adeno-associated viral gene therapy for mucopolysaccharidoses exhibiting neurodegeneration

scientific article

Allogeneic stem cell transplantation does not improve neurological deficits in mucopolysaccharidosis type IIIA mice

scientific article published on 27 July 2010

Endo-lysosomal and autophagic dysfunction: a driving factor in Alzheimer's disease?

scientific article published on 27 December 2016

Functional correction of CNS lesions in an MPS-IIIA mouse model by intracerebral AAV-mediated delivery of sulfamidase and SUMF1 genes

scientific article published on 27 August 2007

Helper-dependent canine adenovirus vector-mediated transgene expression in a neurodegenerative lysosomal storage disorder

scientific article published on 22 September 2011

In vitro characterization of genetically modified embryonic stem cells as a therapy for murine mucopolysaccharidosis type IIIA.

scientific article published on February 2004

Intracerebral gene therapy for mucopolysaccharidosis type IIIB syndrome

scientific article published on 13 July 2017

Lysosomal Dysregulation in the Murine AppNL-G-F/NL-G-F Model of Alzheimer's Disease

scientific article published on 07 January 2020

MPS-IIIA mice acquire autistic behaviours with age.

scientific article published on 8 March 2018

Neonatal Bone Marrow Transplantation in MPS IIIA Mice

scientific article published on 10 August 2012

Open field locomotor activity and anxiety-related behaviors in mucopolysaccharidosis type IIIA mice

scientific article published on 25 March 2008

Reduction in open field activity in the absence of memory deficits in the AppNL-G-F knock-in mouse model of Alzheimer's disease

scientific article published on 5 September 2017

SGSH gene transfer in mucopolysaccharidosis type IIIA mice using canine adenovirus vectors

scientific article published on 14 February 2010

Synthetic Disaccharide Standards Enable Quantitative Analysis of Stored Heparan Sulfate in MPS IIIA Murine Brain Regions

scientific article published on 18 July 2019

Variables influencing fluorimetric N-sulfoglucosamine sulfohydrolase (SGSH) activity measurement in brain homogenates

scientific article published on 22 October 2015

List of works by Adeline A. Lau