List of works by Salima Hacein-Bey-Abina

20 years of gene therapy for SCID.

scientific article

A method to sequence and quantify DNA integration for monitoring outcome in gene therapy ⬇️

scientific article

A modified γ-retrovirus vector for X-linked severe combined immunodeficiency

scientific article

A self-inactivating lentiviral vector for SCID-X1 gene therapy that does not activate LMO2 expression in human T cells

scientific article

A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency

scientific article published in January 2003

Advances in adoptive immunotherapy to accelerate T-cellular immune reconstitution after HLA-incompatible hematopoietic stem cell transplantation

scientific article published on July 2010

Clonal evidence for the transduction of CD34+ cells with lymphomyeloid differentiation potential and self-renewal capacity in the SCID-X1 gene therapy trial

scientific article published on 7 December 2004

Cytokines and culture medium have a major impact on human in vitro T-cell differentiation

scientific article published on 29 April 2011

DNA bar coding and pyrosequencing to analyze adverse events in therapeutic gene transfer

scientific article published on 14 April 2008

Dynamics of gene-modified progenitor cells analyzed by tracking retroviral integration sites in a human SCID-X1 gene therapy trial

scientific article

Efficacy of gene therapy for X-linked severe combined immunodeficiency

scientific article

Failure of SCID-X1 gene therapy in older patients

scientific article

Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1.

scientific article

Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand?

scientific article

Gene Therapy in a Patient with Sickle Cell Disease

scientific article published on March 2017

Gene therapy for immunodeficiency diseases

scientific article published in October 2004

Gene therapy for inherited immunodeficiency

scientific article

Gene therapy for primary adaptive immune deficiencies

scientific article published on June 2011

Gene therapy for primary immunodeficiencies

scientific article published on May 2010

Gene therapy for primary immunodeficiencies.

scientific article

Gene therapy for primary immunodeficiencies: Part 1.

scientific article published on 12 September 2012

Gene therapy for severe combined immunodeficiency

scientific article

Gene therapy of X-linked severe combined immunodeficiency

scientific article

Gene therapy of metabolic diseases

scientific article published on April 2006

Gene therapy of primary T cell immunodeficiencies

scientific article published on 10 April 2013

Gene therapy: X-SCID transgene leukaemogenicity

scientific article

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy

scientific article

INSPIIRED: A Pipeline for Quantitative Analysis of Sites of New DNA Integration in Cellular Genomes

scientific article

Immune reconstitution after haematopoietic stem cell transplantation: obstacles and anticipated progress

scientific article published on 18 September 2009

Improving immune reconstitution while preventing graft-versus-host disease in allogeneic stem cell transplantation

scientific article

Insertion sites in engrafted cells cluster within a limited repertoire of genomic areas after gammaretroviral vector gene therapy

scientific article published on 23 August 2011

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

scientific article

Is normal hematopoiesis maintained solely by long-term multipotent stem cells?

scientific article

LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1

scientific article (publication date: 17 October 2003)

Lentiviral hematopoietic cell gene therapy for X-linked adrenoleukodystrophy

scientific article published in January 2012

Long-term outcome after hematopoietic stem cell transplantation of a single-center cohort of 90 patients with severe combined immunodeficiency

scientific article published on 23 January 2009

Loss of p19Arf in a Rag1(-/-) B-cell precursor population initiates acute B-lymphoblastic leukemia

scientific article

Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome

scientific article published on April 2015

Real-time definition of non-randomness in the distribution of genomic events

scientific article

Restoration of human B-cell differentiation into NOD-SCID mice engrafted with gene-corrected CD34+ cells isolated from Artemis or RAG1-deficient patients

scientific article published on 27 November 2007

Severe combined immunodeficiency. A model disease for molecular immunology and therapy

scientific article

Site- and allele-specific polycomb dysregulation in T-cell leukaemia

scientific article

Specific T cells for the treatment of cytomegalovirus and/or adenovirus in the context of hematopoietic stem cell transplantation

scientific article

Stem cell self-renewal: lessons from bone marrow, gut and iPS toward clinical applications

scientific article published on 29 April 2011

Strategies for retrovirus-based correction of severe, combined immunodeficiency (SCID).

scientific article published in January 2012

Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy

scientific article (publication date: 18 April 2002)

Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia

scientific article

Treatment of an infant with X-linked severe combined immunodeficiency (SCID-X1) by gene therapy in Australia

scientific article

Vector integration is nonrandom and clustered and influences the fate of lymphopoiesis in SCID-X1 gene therapy

scientific article published in August 2007

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