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List of works by Giles V Campion

A randomized placebo-controlled phase 3 trial of an antisense oligonucleotide, drisapersen, in Duchenne muscular dystrophy

scientific article published in December 2017

A sensitive, reproducible and objective immunofluorescence analysis method of dystrophin in individual fibers in samples from patients with duchenne muscular dystrophy

scientific article published in 2014

Author's reply

Comparison of ambulatory capacity and disease progression of Duchenne muscular dystrophy subjects enrolled in the drisapersen DMD114673 study with a matched natural history cohort of subjects on daily corticosteroids

scientific article

Development of the Performance of the Upper Limb module for Duchenne muscular dystrophy

scientific article published on August 2013

Dystrophin quantification: Biological and translational research implications

scientific article

Exon skipping for DMD.

scientific article published on 22 November 2012

Long-Term Efficacy, Safety, and Pharmacokinetics of Drisapersen in Duchenne Muscular Dystrophy: Results from an Open-Label Extension Study

scientific article

Pharmacokinetics and safety of single doses of drisapersen in non-ambulant subjects with Duchenne muscular dystrophy: results of a double-blind randomized clinical trial

scientific article published on 11 September 2013

Placebo-controlled Phase 2 Trial of Drisapersen for Duchenne Muscular Dystrophy

Safety and efficacy of drisapersen for the treatment of Duchenne muscular dystrophy (DEMAND II): an exploratory, randomised, placebo-controlled phase 2 study

scientific article

Stakeholder cooperation to overcome challenges in orphan medicine development: the example of Duchenne muscular dystrophy.

scientific article published on July 2016

Systemic administration of PRO051 in Duchenne's muscular dystrophy

scientific article

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