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List of works by Jeremy Manuel

Force majeure: therapeutic measures in response to restricted supply of imiglucerase (Cerezyme) for patients with Gaucher disease

scientific article published on 4 October 2009

Guidelines for the restart of imiglucerase in patients with Gaucher disease: recommendations from the European Working Group on Gaucher disease

scientific article published on 01 March 2010

Limitations of drug registries to evaluate orphan medicinal products for the treatment of lysosomal storage disorders ⬇️

scientific article

Orphan drug development and the impact on non-medical support groups

scientific article

The European Gaucher Alliance: a survey of member patient organisations' activities, healthcare environments and concerns

scientific article

The legal imperative for treating rare disorders

scientific article

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