List of works - Arran Babbs

2-Arylbenzo[d]oxazole phosphinate esters as second-generation modulators of utrophin for the treatment of Duchenne Muscular Dystrophy

scientific article published on 18 June 2020

A dominant mutation in Snap25 causes impaired vesicle trafficking, sensorimotor gating, and ataxia in the blind-drunk mouse.

scientific article

Diaphragm rescue alone prevents heart dysfunction in dystrophic mice

scientific article published on 09 November 2010

Embryonic myosin is a regeneration marker to monitor utrophin based therapies for DMD

article

Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy

scientific article

Enhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapy

scientific article

From diagnosis to therapy in Duchenne muscular dystrophy

scientific article published on 29 June 2020

Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers.

scientific article published on 2 February 2015

Identification of serum protein biomarkers for utrophin based DMD therapy

scientific article published on 02 March 2017

Micro-utrophin Improves Cardiac and Skeletal Muscle Function of Severely Affected D2/ Mice

scientific article published on 16 October 2018

Prevention of dystrophic pathology in severely affected dystrophin/utrophin-deficient mice by morpholino-oligomer-mediated exon-skipping

scientific article

Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping

scientific article

Second-generation compound for the modulation of utrophin in the therapy of DMD.

scientific article published on May 2015

Synthesis of SMT022357 enantiomers and in vivo evaluation in a Duchenne muscular dystrophy mouse model

scientific article published on 01 January 2020

Temporal transcriptomics suggest that twin-peaking genes reset the clock

scientific article published on 2 November 2015

The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery

scientific article

The potential of utrophin and dystrophin combination therapies for Duchenne muscular dystrophy.

scientific article

List of works by Arran Babbs

2-Arylbenzo[d]oxazole phosphinate esters as second-generation modulators of utrophin for the treatment of Duchenne Muscular Dystrophy

A dominant mutation in Snap25 causes impaired vesicle trafficking, sensorimotor gating, and ataxia in the blind-drunk mouse.

Diaphragm rescue alone prevents heart dysfunction in dystrophic mice

Embryonic myosin is a regeneration marker to monitor utrophin based therapies for DMD

Engineering multiple U7snRNA constructs to induce single and multiexon-skipping for Duchenne muscular dystrophy

Enhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapy

From diagnosis to therapy in Duchenne muscular dystrophy

Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers.

Identification of serum protein biomarkers for utrophin based DMD therapy

Micro-utrophin Improves Cardiac and Skeletal Muscle Function of Severely Affected D2/ Mice

Prevention of dystrophic pathology in severely affected dystrophin/utrophin-deficient mice by morpholino-oligomer-mediated exon-skipping

Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping

Second-generation compound for the modulation of utrophin in the therapy of DMD.

Synthesis of SMT022357 enantiomers and in vivo evaluation in a Duchenne muscular dystrophy mouse model

Temporal transcriptomics suggest that twin-peaking genes reset the clock

The Cellular Processing Capacity Limits the Amounts of Chimeric U7 snRNA Available for Antisense Delivery

The potential of utrophin and dystrophin combination therapies for Duchenne muscular dystrophy.