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List of works by Erin R Burnight

CRISPR-Cas9-Mediated Correction of the 1.02 kb Common Deletion in CLN3 in Induced Pluripotent Stem Cells from Patients with Batten Disease

scientific article published on 01 February 2018

Concise Review: Patient-Specific Stem Cells to Interrogate Inherited Eye Disease

scientific article

Correction of NR2E3 Associated Enhanced S-cone Syndrome Patient-specific iPSCs using CRISPR-Cas9.

scientific article published on 5 April 2019

Development of a Molecularly Stable Gene Therapy Vector for the Treatment of RPGR-Associated X-Linked Retinitis Pigmentosa

scientific article published on 01 August 2019

Gene therapy using stem cells

scientific article

Gene transfer to respiratory epithelia with lentivirus pseudotyped with Jaagsiekte sheep retrovirus envelope glycoprotein

scientific article

Inclusion of Jaagsiekte sheep retrovirus proviral elements markedly increases lentivirus vector pseudotyping efficiency

scientific article

Patient-specific induced pluripotent stem cells (iPSCs) for the study and treatment of retinal degenerative diseases

scientific article

Persistent gene expression in mouse nasal epithelia following feline immunodeficiency virus-based vector gene transfer

scientific article

Stem cells as tools for studying the genetics of inherited retinal degenerations

scientific article published on 11 December 2014

Transcriptional targeting in the airway using novel gene regulatory elements

scientific article

Using Patient-Specific Induced Pluripotent Stem Cells and Wild-Type Mice to Develop a Gene Augmentation-Based Strategy to Treat CLN3-Associated Retinal Degeneration

scientific article published on 11 July 2016

cGMP production of patient-specific iPSCs and photoreceptor precursor cells to treat retinal degenerative blindness

scientific article published on 29 July 2016

piggyBac transposase tools for genome engineering

scientific article published on 30 May 2013

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