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List of works by Aldo Orlacchio

Absence of metabolic cross-correction in Tay-Sachs cells: implications for gene therapy

scientific article published on 28 March 2002

Neural precursor cell cultures from GM2 gangliosidosis animal models recapitulate the biochemical and molecular hallmarks of the brain pathology

scientific article

Neural stem cell gene therapy ameliorates pathology and function in a mouse model of globoid cell leukodystrophy.

scientific article published on October 2011

Specific determination of beta-galactocerebrosidase activity via competitive inhibition of beta-galactosidase

scientific article published on 15 January 2009

Widespread enzymatic correction of CNS tissues by a single intracerebral injection of therapeutic lentiviral vector in leukodystrophy mouse models

scientific article published on 4 March 2010

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