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Frataxin gene editing rescues Friedreich's ataxia pathology in dorsal root ganglia organoid-derived sensory neurons

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Description scientific article published on 21 August 2020
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author: Francesco Nicassio  Marco Rasponi  Vania Broccoli  Chiara Cordiglieri  Franco Taroni  Parisa Tajalli-Tehrani Valverde  Pietro Giuseppe Mazzara  Sharon Muggeo  Marianna Paulis 

Publication date August 21, 2020
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