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Ataluren-driven Restoration of Shwachman-Bodian-Diamond Syndrome Protein Function in Shwachman-Diamond Syndrome Bone Marrow Cells

scientific article

Author/s

author: Valentino Bezzerri, Giovanna D'Amico, Piero Farruggia, Claudio Sorio, Simone Cesaro, Andrea Biondi

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Work details

Publication date
December 29, 2017
- -
Language
English

Copyright status