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Sustained knockdown of a disease-causing gene in patient-specific induced pluripotent stem cells using lentiviral vector-based gene therapy

scientific article published on 07 August 2013

Author/s

author: Axel Schambach, Daniela Zychlinski, Malte Sgodda, Christian Herr, Guangming Wu, Jeffrey Teckman, Tobias Cantz, Hans Schöler, Doris Steinemann

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Publication date
August 7, 2013
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