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AON-mediated Exon Skipping Restores Ciliation in Fibroblasts Harboring the Common Leber Congenital Amaurosis CEP290 Mutation

scientific article

Author/s

author: Jean-michel Rozet, Xavier Gérard, Eduardo Silva, Josseline Kaplan, Isabelle Perrault, Arnold Munnich, Sylvain Hanein

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Work details

Publication date
June 26, 2012
- -
Language
English

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