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Prevalence of anti-adeno-associated virus serotype 8 neutralizing antibodies and arylsulfatase B cross-reactive immunologic material in mucopolysaccharidosis VI patient candidates for a gene therapy trial.

scientific article

Author/s

author: Marco Savarese, Rossella Parini, Vincenzo Nigro, Nicola Brunetti-Pierri, Alberto Auricchio, John Hopwood, Ans van der Ploeg, Simona Fecarotta

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Publication date
March 1, 2015
- -
Language
English

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