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EPI-743 reverses the progression of the pediatric mitochondrial disease--genetically defined Leigh Syndrome.

scientific article

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author: Enrico Bertini, Fiorella Piemonte, Anna Pastore, Giulia Tozzi, Carlo Dionisi-Vici, Giuseppe Pontrelli, Diego Martinelli, Michela Catteruccia, Thomas H Miller

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Publication date
September 10, 2012
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