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Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial.

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author: Stephanie G Sumner-Jones  Ruaridh Buchan  Maria H Dewar  Paula Carvelli  Jemyr Gavino  Roberto Calcedo  Hala I Elgmati  Sabrina Gea-Sorli  Rosanna F Featherstone  Michelle C Manvell  Uta Griesenbach  Paul Lloyd-Evans  Laura Hyndman  Laura J Moyce  Cuixiang Meng  Tina Osadolor  Hazel Milligan  Gina Rivellini  Kamila M Pytel  Javier Parra-Leiton  Ronald K Scheule  Samia Soussi  Najwa Soussi  Nicholas J Simmonds  Rosa P Ureta  UK Cystic Fibrosis Gene Therapy Consortium  Marguerite Y Wasowicz  Paul Wolstenholme-Hogg  Deborah Gill  Brian Keogh  Stephen C Hyde  Katie J Bayfield  David D Collie  Dominique McCormick  Alexandra L Quittner  Tracy Higgins  Diana Bilton  Maria P Limberis  Gerry McLachlan  Samantha Hodges  James Wilson  Emma K Punch  Jackie Donovan  Mario Liong  Steve Cunningham  David J. Porteous  Minna Turkkila  Deborah Ashby 

Publication date July 3, 2015
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