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Enzyme replacement therapy for mucopolysaccharidosis VI: evaluation of long-term pulmonary function in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase

scientific article

Author/s

author: Robert D. Steiner, Kenneth I. Berger, Ida Vanessa D Schwartz, Roberto Giugliani, Paul R Harmatz, David Ketteridge, Nathalie Guffon, Elisa Leão Teles, Stuart J Swiedler, Edmond Wraith, Laila Arash, Maurizio Scarpa, Barbara Plecko, Chester B Whitley, Paige Kaplan, Celeste Decker, John Hopwood

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Work details

Publication date
February 6, 2010
- -
Language
English

Copyright status