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A randomised, double-blind, placebo-controlled trial of repeated nebulisation of non-viral cystic fibrosis transmembrane conductance regulator (CFTR) gene therapy in patients with cystic fibrosis

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Description scientific article
Author/s

author: Stephanie G Sumner-Jones  Ruaridh Buchan  Maria H Dewar  Paula Carvelli  Roberto Calcedo  Jemyr Gavino  Hala I Elgmati  Sabrina Gea-Sorli  Rosanna F Featherstone  Michelle C Manvell  Laura Hyndman  Paul Lloyd-Evans  Uta Griesenbach  Laura J Moyce  Cuixiang Meng  Tina Osadolor  Gina Rivellini  Hazel Milligan  Javier Parra-Leiton  Kamila M Pytel  Ronald K Scheule  Samia Soussi  Nicholas J Simmonds  Najwa Soussi  Rosa P Ureta  Marguerite Y Wasowicz  Paul Wolstenholme-Hogg  Deborah Gill  Brian Keogh  Stephen C Hyde  Katie J Bayfield  David D Collie  Dominique McCormick  Alexandra L Quittner  Tracy Higgins  Diana Bilton  Maria P Limberis  Gerry McLachlan  Samantha Hodges  James Wilson  Emma K Punch  Jackie Donovan  Mario Liong  David J. Porteous  Minna Turkkila  Deborah Ashby 

Publication date July 2016
Language English
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